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Future AAVenues for In Utero Gene Therapy.

Abstract：

:Fetal gene therapy using safe and effective viral vectors no longer remains a distant prospect. Recently in Nature Medicine, Massaro et al. (2018) demonstrated that prenatal intracranial injection of a viral vector results in improved neurologic function, raising the intriguing possibility that in utero gene therapy may be approaching clinical applications.

journal_name

Cell Stem Cell

journal_title

Cell stem cell

authors

MacKenzie TC

doi

10.1016/j.stem.2018.08.010

subject

Has Abstract

pub_date

2018-09-06 00:00:00

pages

320-321

issue

3

eissn

1934-5909

issn

1875-9777

pii

S1934-5909(18)30395-3

journal_volume

23

pub_type

评论,杂志文章

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