Abstract:
:Blackfan-Diamond anemia (BDA) is a rare hypoproliferative anemia occurring in infancy or in early childhood. Patients who fail on usual doses of steroids did not achieve remission with other pharmacological agents. Claims that other molecules such as cyclosporin A (CSA) or antithymocyte globulin (ATG) are effective require substantiation. We treated four transfusion-dependent, steroid-unresponsive BDA patients with ATG and methylprednisolone (MP). Only a transient response was obtained in one case. None of these patients responded to high-dose intravenous immunoglobulins (HDIg) or CSA.
journal_name
Haematologicajournal_title
Haematologicaauthors
Bejaoui M,Fitouri Z,Sfar MT,Lakhoua Rsubject
Has Abstractpub_date
1993-01-01 00:00:00pages
38-9issue
1eissn
0390-6078issn
1592-8721journal_volume
78pub_type
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