Hematopoietic Stem Cell Transplantation for Severe Combined Immunodeficiency (SCID).

Abstract:

:Severe Combined Immunodeficiencies (SCID) are a heterogeneous group of monogenetic diseases. We describe the typical clinical presentation of patients with SCID as well as basic principles in diagnosis and therapy by hematopoietic stem cell transplantation. Therapeutic strategies may differ between subtypes and the inherent reduced capacity or inablility to reject a graft have to be considered.

journal_name

Front Pediatr

journal_title

Frontiers in pediatrics

authors

Haddad E,Hoenig M

doi

10.3389/fped.2019.00481

subject

Has Abstract

pub_date

2019-11-19 00:00:00

pages

481

issn

2296-2360

journal_volume

7

pub_type

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