Abstract:
:The ability to evaluate effects of factors on outcomes is increasingly important for studies that control some but not all of the factors. Although important advances have been made in methods of analysis for such partially controlled studies, work on designs has been limited. To help understand why, we review the main designs that have been used for such partially controlled studies. Based on the review, we give two complementary reasons that explain the limited work on such designs, and suggest a new direction in this area.
journal_name
Stat Methods Med Resjournal_title
Statistical methods in medical researchauthors
Li F,Frangakis CEdoi
10.1191/0962280205sm405oasubject
Has Abstractpub_date
2005-08-01 00:00:00pages
417-31issue
4eissn
0962-2802issn
1477-0334journal_volume
14pub_type
杂志文章abstract::In this study, we discuss a decision theoretic or fully Bayesian approach to the sample size question in clinical trials with binary responses. Data are assumed to come from two binomial distributions. A Dirichlet distribution is assumed to describe prior knowledge of the two success probabilities p1 and p2. The param...
journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280211399562
更新日期:2013-12-01 00:00:00
abstract::The probability model for periodic screening was extended to provide statistical inference for sensitivity depending on sojourn time, in which the sensitivity was modeled as a function of time spent in the preclinical state and the sojourn time. The likelihood function with the proposed sensitivity model was then eval...
journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280212465499
更新日期:2016-04-01 00:00:00
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journal_title:Statistical methods in medical research
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doi:10.1177/0962280220958177
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280218779408
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abstract::In this paper, a new allocation rule for treatment assignments in sequential clinical trials is proposed. The stratified and randomized play-the-winner rule (SRPWR) is an extension of the randomized play-the-winner rule to more than two treatments. It is applicable to cases where the probabilities of success of a trea...
journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280207081606
更新日期:2008-12-01 00:00:00
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280218784726
更新日期:2019-08-01 00:00:00
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280217704451
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journal_title:Statistical methods in medical research
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doi:10.1177/0962280213503928
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280210379365
更新日期:2012-08-01 00:00:00
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journal_title:Statistical methods in medical research
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journal_title:Statistical methods in medical research
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doi:10.1177/0962280218788383
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280214527384
更新日期:2014-12-01 00:00:00
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journal_title:Statistical methods in medical research
pub_type: 杂志文章,评审
doi:10.1191/0962280202sm290ra
更新日期:2002-08-01 00:00:00
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/096228020101000305
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280214526193
更新日期:2016-12-01 00:00:00
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journal_title:Statistical methods in medical research
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doi:10.1177/0962280217736342
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1191/0962280205sm413oa
更新日期:2005-10-01 00:00:00
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280217735560
更新日期:2019-03-01 00:00:00
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journal_title:Statistical methods in medical research
pub_type: 杂志文章,评审
doi:10.1191/0962280204sm352ra
更新日期:2004-02-01 00:00:00
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journal_title:Statistical methods in medical research
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doi:10.1177/0962280212466089
更新日期:2016-04-01 00:00:00
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journal_title:Statistical methods in medical research
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
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更新日期:2018-01-01 00:00:00
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journal_title:Statistical methods in medical research
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更新日期:2019-07-01 00:00:00
abstract::The semiparametric Cox regression model is often fitted in the modeling of survival data. One of its main advantages is the ease of interpretation, as long as the hazards rates for two individuals do not vary over time. In practice the proportionality assumption of the hazards may not be true in some situations. In ad...
journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280219883905
更新日期:2020-08-01 00:00:00
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journal_title:Statistical methods in medical research
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journal_title:Statistical methods in medical research
pub_type: 杂志文章
doi:10.1177/0962280214527385
更新日期:2014-12-01 00:00:00
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